Orphan medicinal products
Orphan medicinal products are intended for the analysis, prevention or treatment of dangerous or very serious conditions that affect no more than 5 in 10,000 people in the European Union. Patients suffering from rare diseases deserve the same quality of treatment as other patients within the European Union. Given the small numbers of patients affected by rare diseases, the pharmaceutical industry has been unwilling in the past to invest in the research and development of medicinal products to treat them. The EU introduced new legislation in 2000 with the aim of providing incentives for the development of medicines for rare diseases (so-called orphan medicinal products).
- Orphan designation
- Medicines for rare diseases
Related Conference of Orphan medicinal products
July 21-22, 2025
11th International Conference on Antimicrobials & Antibiotic Resistance
Vancouver, Canada
August 25-26, 2025
11th International Conference on Pharmaceutical Regulatory Affairs and IPR
Vancouver, Canada
September 08-09, 2025
26th International Conference and Exhibition on Pharmaceutics & Novel Drug Delivery Systems
Frankfurt, Germany
September 08-09, 2025
13th International Conference and Exhibition on Natural Products and Medicinal Plants Research
Frankfurt, Germany
September 15-16, 2025
42nd International Conference on Drug Discovery and Drug delivery system
Paris, France
September 22-23, 2025
20th International Conference on Pharmaceutical Formulations & Drug Delivery
Toronto, Canada
September 23-24, 2025
10th International Conference on Future Pharma and Innovations
Amsterdam, Netherlands
November 13-14, 2025
28th International Conference and Exhibition on Pharmaceutical Formulations
Paris, France
November 13-14, 2025
21st International Conference on Pharmaceutical Chemistry
Aix-en-Provence, France
November 25-26, 2025
4th World Congress on Medicinal Chemistry and Computer Aided Drug Design
Aix-en-Provence, France
November 27-28, 2025
4th World Conference on Pharma Industry and Medical Devices
Zurich, Switzerland
January 28-29, 2026
23rd International Pharmaceutical Sciences & Life Saving Drugs
Bangkok, Thailand
Orphan medicinal products Conference Speakers
Recommended Sessions
- Allergic and immunologic disorders
- Challenges in rare disease development
- Clinical trials and treatment
- Gene therapy for rare diseases
- Infectious diseases
- Orphan Diseases and public health
- Orphan drugs potentiality
- Orphan medicinal products
- Rare diseases in blood stream
- Rare infectious diseases and immune deficiencies
- Rare mental and behavioral diseases
- Rare neurological diseases
- Rare nutritional and metabolic diseases
- Rare pediatric diseases
- Treatment and advanced therapies for rare diseases
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