Rare Diseases & Orphan Drugs

Orphan Drug Pricing and Reimbursement Strategies

Orphan drugs for rare diseases are often expensive due to the high cost of research and development and the small patient populations they serve. Pricing and reimbursement strategies for orphan drugs must balance the need to recoup development costs with ensuring access for patients. Governments and payers have implemented various strategies, such as price controls, discounts, and value-based pricing, to manage the cost of orphan drugs. Additionally, patient assistance programs, such as copay assistance and free drug programs, help ensure that patients can access treatments. Balancing affordability and access to treatments for patients with rare diseases remains an ongoing challenge for policymakers and stakeholders.